Mucopolysaccharidosis Type I (MPS I) is a rare genetic disorder that disrupts the body's ability to break down glycosaminoglycans (GAGs), leading to severe organ and tissue damage. While traditional treatments like enzyme replacement therapy (ERT) have provided significant benefits, the search for more effective and long-lasting therapies continues. In this article, we will explore...

    Mucopolysaccharidosis Type I (MPS I) is a rare genetic disorder that disrupts the body’s ability to break down GAGs, leading to serious health issues like organ enlargement, skeletal abnormalities, and neurological decline. Although MPS I is considered a challenging condition to treat, advances in medical science have led to significant improvements in care. Traditional...