Breaking New Ground in MPS I Treatment: The Shift from ERT to Gene-Based Therapies
    Mucopolysaccharidosis Type I (MPS I) is a rare genetic disorder that disrupts the body’s ability to break down GAGs, leading to serious health issues like organ enlargement, skeletal abnormalities, and neurological decline. Although MPS I is considered a challenging condition to treat, advances in medical science have led to significant improvements in care. Traditional...
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