Paroxysmal Nocturnal Hemoglobinuria: Pipeline Innovations and Market Growth Paroxysmal Nocturnal Hemoglobinuria (PNH) stands as a rare, acquired, life-threatening hematological condition characterized by complement-driven hemolysis, bone marrow insufficiency, and thrombotic events. This disorder originates from mutations in the PIGA gene, causing inadequate protective proteins on red blood cell membranes. The lack of these crucial protective components leads the immune...