Mucopolysaccharidosis Type I Treatment Pipeline: 4 Promising Therapies on the Way
    Mucopolysaccharidosis Type I (MPS I) represents one of the most challenging inherited metabolic disorders, affecting approximately 1 in 100,000 births worldwide. This rare genetic condition occurs when the body lacks sufficient alpha-L-iduronidase enzyme, leading to the harmful accumulation of glycosaminoglycans in cells throughout the body. While current treatments have...
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